STRIDE STUDY A Study in Subjects With LOPD Who Are Currently Being Treated With ERT
VAL-1221 for Pompe Disease VAL-1221 Delivered Intravenously in Ambulatory and Ventilator-free Patients With Late-Onset Pompe Disease
neoGAA COMET Study to Compare the Efficacy and Safety of Enzyme Replacement Therapies neoGAA and Alglucosidase Alfa Administered Every Other Week in Patients With Late-onset Pompe Disease Who Have Not Been Previously Treated for Pompe Disease
neoGAA Mini COMET A Study to Assess Safety and Efficacy of NeoGAA Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa
FOR A COMPLETE LIST OF CLINICAL PLEASE CLICK ON THE LINK BELOW: