by United Pompe | Jan 18, 2016 | News
IPA Summary of Genzyme Press Release The Genzyme press release about the Pompe program put on GSD net by our IPA board member Allan Muir a week ago will probably raise some questions. With a summary description IPA would like to answer them. Genzyme informed us about...
by United Pompe | Jan 18, 2016 | News
Letter From Jan van Heek On Saturday, March 9th, 2002, I will be speaking at the VSN (The Dutch Muscular Dystrophy Association, Vereniging Spierziekten Nederland) Annual Patient Conference in The Netherlands. At the conference I will provide a general overview of...
by United Pompe | Jan 18, 2016 | News
Rescue of enzyme deficiency in embryonic diaphragm in a mouse
by United Pompe | Jan 18, 2016 | News
Long-Term Intravenous Treatment of Pompe Disease With Recombinant Human a-Glucosidase From Milk
by United Pompe | Jan 18, 2016 | News
Myozyme Produced at the 2000 L Bioreactor Scale to Receive Accelerated Approval Date: November 17, 2008 New PDUFA Date Set for February 28, 2009 Genzyme Corporation (Nasdaq: GENZ) today announced that the FDA plans an Accelerated Approval for Myozyme® (alglucosidase...
by United Pompe | Jan 18, 2016 | News
The Team Behind the Treatment by Marsha A. Green Yamila Jimenez is a 3-year-old walking miracle. She has Pompe (pronounced pom-PAY) disease, a rare genetic disease that means her body is unable to produce a vital enzyme needed to turn the sugar (glycogen) in her...
