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MTAP Fact Sheet July 2007

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Pompe Program Update May 2007 There are two studies to further evaluate Myozyme® (alglucosidase alfa) that will be conducted as part of Genzyme’s postmarketing commitments (PMC) to the FDA. A postmarketing commitment is an agreement between a regulatory agency and a...

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GENZYME POMPE PROGRAM APRIL 2007

In an effort to complete the AGLU02704 study (Late-Onset Treatment Study, LOTS) as responsibly as possible, Genzyme has amended the study protocol to incorporate the use of an adaptive design. Genzyme utilized this method to help ensure a conclusive trial outcome in...

Expensive drug gives hope to rare disease sufferer